JUNE 2025 - PEDIATRIC BLOOD AND CANCER

Accelerating Drug Development for Neuroblastoma: Consensus Statement From the Third Neuroblastoma Drug Development Strategy Forum

Steven G. DuBois, Lucas Moreno, John Anderson, Shahab Asgharzadeh, Ro Bagatell, Maja Beck-Popovic, Jen Belle, Pablo Berlanga, Nick J. Bird, Louis Chesler, Adam Durbin, Angelika Eggert, Martin Eilers, Sara M. Federico, Matthias Fischer, Susanne A. Gatz, Rani E. George, Sally George, Kelly C. Goldsmith, Juliet Gray, Andras Heczey, Meredith S. Irwin, Leona Knox, Holger N. Lode, Donna Ludwinski, Margaret E. Macy, Robbie G. Majzner, John M. Maris, Shakeel Modak, Jan J. Molenaar, Daniel A. Morgenstern, Yael P. Mossé, Cormac Owens, C. Patrick Reynolds, Claudia Rossig, Gudrun Schleiermacher, Liz Scott, Paul M. Sondel, Frank Speleman, Max van Noesel, Frank Westermann, Judith Wienke, Adam J. Wolpaw, Julie R. Park, Andrew D. J. Pearson

FIND ACCESS TO PUBLICATION HERE: https://onlinelibrary.wiley.com/doi/10.1002/pbc.31831

FEBRUARY 2025 - EUROPEAN JOURNAL OF CANCER

Paediatric strategy forum for medicinal product development in diffuse midline gliomas in children and adolescents ACCELERATE in collaboration with the European Medicines Agency with participation of the Food and Drug Administration

Andrew DJ Pearson, Sabine Mueller, Mariella G. Filbin, Jacques Grill, Cynthia Hawkins, Chris Jones, Martha Donoghue, Nicole Drezner, Susan Weiner, Mark Russo, Matthew D. Dun, Joshua E. Allen, Marta Alonso, Ely Benaim, Vickie Buenger, Teresa de Rojas, Keith Desserich, Elizabeth Fox, John Friend, Julia Glade Bender, Darren Hargrave, Michael Jensen, Olga Kholmanskikh, Mark W. Kieran, Holly Knoderer, Carl Koschmann, Giovanni Lesa, Franca Ligas, Nir Lipsman, Donna Ludwinski, Lynley Marshall, Joe McDonough, Adrian G. McNicholl, David Mirsky, Michelle Monje, Karsten Nysom, Alberto Pappo, Amy Rosenfield, Nicole Scobie, Joan Slaughter, Malcolm Smith, Mark Souweidane, Karin Straathof, Lisa Ward, Brenda Weigel, Dmitry Zamoryakhin, Dominik Karres, Gilles Vassal

FIND ACCESS TO PUBLICATION HERE: https://www.ejcancer.com/article/S0959-8049(25)00011-5/fulltext

DECEMBER 2024 - EUROPEAN JOURNAL OF CANCER

Stakeholder Perspectives on Randomized Clinical Trials for Children With Poor-Prognosis Cancers

Nicholas Bird, Nicole Scobie; Pablo Berlanga, Patricia Blanc, Vickie Buenger, Quentin Campbell-Hewson, Michela Casanova, Steven DuBois Julia Glace Bender, Ann Graham, Delphine Heenen, Christina Ip-Toma, Donna Ludwinski, Lucas Moreno, Donna Neuberg, Antonia Palmer, Xavier Paoletti, Willemijn Plieger-van Solkema, Gregory Reaman Teresa de Rojas, Claudia Rossig, Anja Schiel, Sara Wakeling, Gilles Vassal, Andrew Pearson, Leona Knox

FIND ACCESS TO PUBLICATION HERE: https://jamanetwork.com/journals/jamanetworkopen/fullarticle/2827560

JUNE 2024 - EUROPEAN JOURNAL OF CANCER

Paediatric Strategy Forum for Medicinal Product Development of PI3-K, mTOR, AKT and GSK3β Inhibitors in Children and Adolescents with Cancer

Andrew DJ Pearson, Steven G DuBois, Margaret E Macy, Teresa de Rojas, Martha Donoghue, Susan Weiner, Holly Knoderer, Ronald Bernardi, Vickie Buenger, Guillaume Canaud, Lewis Cantley, John Chung, Elizabeth Fox, John Friend, Julia Glade-Bender, Igor Gorbatchevsky, Lia Gore, Abha Gupta, Douglas S Hawkins, Dejan Juric, Leigh Anna Lang, Danielle Leach, Danny Liaw, Giovanni Lesa, Franca Ligas, Gavin Lindberg, Wendy Lindberg, Donna Ludwinski, Lynley Marshall, Andrew Mazar, Joe McDonough, Karsten Nysom, Christopher Ours, Alberto Pappo, D William Parsons, Amy Rosenfeld, Nicole Scobie, Malcolm Smith, Danielle Taylor, Brenda Weigel, Amy Weinstein, Dominik Karres, Gilles Vassal

FIND ACCESS TO PUBLICATION HERE: https://www.sciencedirect.com/science/article/abs/pii/S0959804923003027

APRIL 2024 - DAY ONE BIOPHARMCEUTICALS

Advancing Pediatric Cancer Research and Drug Development Through Multistakeholder Collaboration: A Framework Based on the Tovorafenib Journey

Annette Bakker, Caitlyn Barrett, Upal Basu Roy, John Hopper, Marc Hurlbert, Christa Kerkorian, Mark Kieran,  Donna Ludwinski, Amy Weinstein

FIND ACCESS TO PUBLICATION HERE: https://www.dayonebio.com/wp-content/uploads/Multistakeholder-Collaboration-in-Pediatric-Cancer-April-2024.pdf

JUNE 21, 2023 - EUROPEAN JOURNAL OF CANCER

Paediatric Strategy Forum for Medicinal Product Development of DNA Damage Response Pathway Inhibitors in Children and Adolescents with Cancer ACCELERATE in collaboration with the European Medicines Agency With participation of the Food and Drug Administration

Andrew DJ Pearson, Sara Federico, Susanne A Gatz, Michael Ortiz, Giovanni Lesa, Nicole Scobie, Ioannis Gounaris, Susan L Weiner, Brenda Weigel, TJ Unger, Elizabeth Stewart, Malcolm Smith, Emily K Slotkin, Gregory Reaman, Alberto Pappo, Karsten Nysom, Koen Norga, Joe McDonough, Lynley V Marshall, Donna Ludwinski, Gilles Vassal

FIND ACCESS TO PUBLICATION HERE: https://www.sciencedirect.com/science/article/abs/pii/S0959804923003027

NOVEMBER 2022 - PEDIATRIC CANCER THERAPEUTICS DEVELOPMENT

Role of Patients and Advocates in Cancer Therapeutics Development

Donna Ludwinski, Nicole Scobie, Leona Knox

FIND ACCESS TO PUBLICATION HERE: https://link.springer.com/chapter/10.1007/978-3-031-06357-2_9

SEPTEMBER 2022 - EUROPEAN JOURNAL OF CANCER

Paediatric Strategy Forum for medicinal product development of multi-targeted kinase inhibitors in bone sarcomas: ACCELERATE in collaboration with the European Medicines Agency with participation of the Food and Drug Administration

Andrew DJ.Pearson, Nathalie Gaspar, Katherine Janeway, Quentin Campbell-Hewson, Elizabeth R. Lawlore, Chris Copland, Dominik Karresh, Koen Norga, Fawzi Benzaghoul, Susan Weiner, Brenda Weigel, Aaron R. Weiss, Sandra J. Strauss, Malcolm Smith, Bhuvana A. Setty, Nita Seibel, Nicole Scobie, Alberto Pappo, Chinyere E. Okpara, Karsten Nysom, Joe McDonough, Lynley V. Marshall, Donna Ludwinski, Franca Ligas, Giovanni Lesa, Steen Knudsen, John Kauh, Antony Hsieh, Delphine Heenen, Douglas S. Hawkins, Ann Graham, Edward Garmey, Steven G. DuBois, Elizabeth Fox, Martha Donoghue, Teresa de Rojas, John Chung, Michela Casanova, Bernadette Brennan, Michael Bishop, Vickie Buenger, Gregory Reaman, Gilles Vassal

ACCESS FULL PAPER HERE: https://www.sciencedirect.com/science/article/pii/S0959804922003598

AUGUST 2022 - JOURNAL OF CLINICAL ONCOLOGY

The Critical Role of Academic Clinical Trials in Pediatric Cancer Drug Approvals: Design, Conduct, and Fit for Purpose Data for Positive Regulatory Decisions

Bram De Wilde, Elly Barry, Elizabeth Fox , Dominik Karres, Mark Kieran, John Manlay, Donna Ludwinski, Gregory Reaman, and Pamela Kearns

ACCESS FULL PAPER HERE: https://ascopubs.org/doi/abs/10.1200/JCO.22.00033

JUNE 2022 - PEDIATRIC BLOOD AND CANCER

A systematic literature review to identify ethical, legal, and social responsibilities of nonprofit organizations when funding clinical trials in pediatric cancer

Vasiliki Rahimzadeh, Susan Wolfert, Vickie Buenger, Cindy Campbell, Robin French, Donna Ludwinski, Amy Weinstein, Caitlyn Barrett

ACCESS FULL PAPER HERE: https://onlinelibrary.wiley.com/doi/epdf/10.1002/pbc.29854

APRIL 2022 - PEDIATRIC BLOOD AND CANCER

To transplant, or not to transplant? That is the question. A patient advocate evaluation of autologous stem cell transplant in neuroblastoma

Nicholas Bird, Nicole Scobie, Antonia Palmer, Donna Ludwinski

ACCESS FULL PAPER HERE: https://onlinelibrary.wiley.com/doi/10.1002/pbc.29663

NOVEMBER 2021 - EUROPEAN JOURNAL OF CANCER

Paediatric Strategy Forum for medicinal product development of chimeric antigen receptor T-cells in children and adolescents with cancer

Andrew DJ. Pearson, Claudia Rossig, Crystal Mackall, Nirali N. Shah, Andre Baruchel, Gregory Reaman, Rosanna Ricafort, Delphine Heenen, Abraham Bassan, Michael Berntgen, Nick Bird, Eric Bleickardt, Najat Bouchkouj, Peter Bross, Carrie Brownstein m, Sarah Beaussant Cohen n , Teresa de Rojas, Lori Ehrlich, Elizabeth Fox, Stephen Gottschalk, Linda Hanssens, Douglas S. Hawkins, Ivan D. Horak, Danielle H. Taylor, Courtney Johnson, Dominik Karres, Franca Ligas, Donna Ludwinski, Maksim Mamonkin, Lynley Marshall, Behzad K. Masouleh, Yousif Matloub, Shannon Maude, Joe McDonough, Veronique Minard-Colin, Koen Norga, Karsten Nysom, Alberto Pappo, Laura Pearce, Rob Pieters, Martin Pule, Alfonso Quinta´s-Cardama, Nick Richardson, Martina Schu¨ßler-Lenz, Nicole Scobie, Martina A. Sersch, Malcolm A. Smith, Jaroslav Sterba, Sarah K. Tasian, Brenda Weigel, Susan L. Weiner, Christian Michel Zwaan, Giovanni Lesa, Gilles Vassal

ACCESS FULL PAPER HERE: https://www.ejcancer.com/action/showPdf?pii=S0959-8049%2821%2901170-9

NOVEMBER 2021 - JOURNAL OF CLINICAL ONCOLOGY

When Innovation and Commercialization Collide: A Patient Advocate View in Neuroblastoma

Nicholas Bird, Leona Knox, Antonia Palmer, Delphine Heenen, Patricia Blanc, Nicole Scobie, Donna Ludwinski

ACCESS FULL PAPER HERE:  https://ascopubs.org/doi/pdf/10.1200/JCO.21.01916

AUGUST 2021 - MOLECULAR CANCER THERAPEUTICS, VOLUME 20, ISSUE 8

International Consensus on Minimum Preclinical Testing Requirements for the Development of Innovative Therapies For Children and Adolescents with Cancer

Gilles Vassal, Peter J. Houghton, Stefan M. Pfister, Malcolm A. Smith, Huib N. Caron, Xiao-Nan Li, David J. Shields, Olaf Witt, Jan J. Molenaar, Sara Colombetti, Julia Schüler and Lou F. Stancato; CREDITED: Donna Ludwinski

FULL PAPER CAN BE ACCESSED HERE: https://solvingkidscancer.org/wp-content/uploads/2021/08/MCT-08-2021-CONSENSUS-PAPER.pdf

MARCH 2021 - EUROPEAN JOURNAL OF CANCER, VOLUME 146

Bromodomain and Extra-terminal Inhibitors—A Consensus Prioritisation After the Paediatric Strategy Forum for Medicinal Product Development of Epigenetic Modifiers in Children—ACCELERATE

Andrew DJ.Pearson, Steven G.DuBois, Vickie Buenger, Mark Kieran, KimberlyStegmaier, Pratiti Bandopadhayay, Kelly Bennette, Franck Bourdeaut, Patrick A.Brown, Louis Chesler, Jessica Clymer, Elizabeth Foxi, Christopher A. French, Eva Germovsek, Francis J.Giles, Julia G. Benderm, Maureen M.Hattersley, Donna Ludwinski, Katarina Luptakova, John Maris, Joe McDonough, Zariana Nikolova, Malcolm Smith, Athanasios C.Tsiatis, Rajeev Vibhakar, Susan Weiner, Joanna S.Yi, Fred Zheng, Gilles Vassal

FULL PAPER CAN BE ACCESSED HERE: https://www.sciencedirect.com/science/article/pii/S0959804921000307

NOVEMBER 2020 - EUROPEAN JOURNAL OF CANCER, VOLUME 139

Paediatric Strategy Forum for Medicinal Product Development of Epigenetic Modifiers for Children - ACCELERATE in collaboration with the European Medicines Agency with participation of the Food and Drug Administration

Andrew DJ. Pearson, Kimberly Stegmaier, Franck Bourdeaut, Gregory Reaman, Delphine Heenen, Michael L. Meyers, Scott A. Armstrong, Patrick Brown, Daniel De Carvalho, Nada Jabado, Lynley Marshall, Miguel Rivera, Malcolm Smith, Peter C. Adamson, Amy Barone, Christian Baumann, Samuel Blackman, Vickie Buenger, Martha Donoghue, Aundrietta D. Duncan, Elizabeth Fox, Brian Gadbaw, Maureen Hattersley, Peter Ho, Ira Jacobs, Michael J. Kelly, Mark Kieran, Giovanni Lesa, Franca Ligas, Donna Ludwinski, Joe McDonough, Zariana Nikolova, Koen Norga, Adrian Senderowicz, Tilmann Taube, Susan Weiner, Dominik Karres, Gilles Vassal

ACCESS THE FULL PAPER HERE: https://www.ejcancer.com/article/S0959-8049(20)30465-2/fulltext

AUGUST 2020 - PIZZO AND POPLACK'S PEDIATRIC ONCOLOGY: EIGHTH EDITION

Chapter 48 - The Other Side of the Bed: What Providers Can Learn from Listening to Patients and their Families

Donna Ludwinski, Vikas Kundra, Nancy Goodman, Leona Knox, and Elena Gerasimov

TEXTBOOK IS AVAILABLE FOR PURCHASE HERE: https://shop.lww.com/Pizzo---Poplack-s-Pediatric-Oncology/p/9781975124793

SEPTEMBER 2020 - PEDIATRIC BLOOD AND CANCER, VOLUME 67, ISSUE 9

Pediatric Cancer Research: Surviving COVID-19

Jeffery J. Auletta, Peter C. Adamson, Jonathan E. Agin, Pamela Kearns, Scott Kennedy, Mark W. Kieran, Donna M. Ludwinski, Leona J. Knox, Kristi McKay, Pia Rhiner, Carol J. Thiele, Timothy P. Cripe

ACCESS THE FULL PAPER HERE: https://onlinelibrary.wiley.com/doi/10.1002/pbc.28435

NOVEMBER 2017 - PEDIATRIC BLOOD AND CANCER, VOLUME 64, ISSUE S3

SIOP Abstracts: O-137 Charity Role in International Paediatric Cancer Clinical Trials

S. Kennedy, D. Ludwinski, S. Richards, L. Knox, J. Rogers

ACCESS ALL ABSTRACTS HERE: https://onlinelibrary.wiley.com/doi/full/10.1002/pbc.26772#

NOVEMBER 2017 - PEDIATRIC BLOOD AND CANCER, VOLUME 64, ISSUE S3

SIOP Abstracts: P-389 Drug Development and Market Challenge - Charity Stakeholder Perspective

S. Richards, L. Knox, N. Bird, J. Rogers, D. Ludwinski

ACCESS ALL ABSTRACTS HERE: https://onlinelibrary.wiley.com/doi/full/10.1002/pbc.26772#

OCTOBER 2011 - PEDIATRIC BLOOD AND CANCER, VOLUME 57, ISSUE 5

43RD CONGRESS OF THE INTERNATIONAL SOCIETY OF PAEDIATRIC ONCOLOGY (SIOP) 2011 ABSTRACTS

Web-Based Neuroblastoma Research Information for Parents: A Model for International Collaboration of Pediatric Cancer Non-Profits

Donna Ludwinski, John Rogers, Graeme Tucker

ACCESS ALL ABSTRACTS HERE: https://onlinelibrary.wiley.com/doi/full/10.1002/pbc.23299